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Applications

Applications by research stage, cell type and RNA class

Self-delivering antisense oligonucleotides silence a target in cells that resist transfection, in 3D models and in vivo, with no transfection reagent. Each entry leads to the guide or the product page written for it.

By research stage

Three stages, one platform

The same designed sequence serves a gene function study, a target validation and a patient-derived model; what changes is the cell, the read-out and the scale.

  1. 01

    Basic fundamental research

    Start from a gene symbol. The reference pages carry the transcript, its isoforms and where it is expressed, and the design reads the same record.

    • Gene function studies
    • Pathway dissection
    • RNA biology discovery
    • Mechanism of action
  2. 02

    Translational research

    Knock the target down in primary cells and in vivo without a carrier, with the controls and read-outs each cell type guide names.

    • Target validation
    • Biomarker discovery
    • Disease modeling
    • Preclinical studies
  3. 03

    Preclinical research

    Patient-derived models and candidate testing at the scale the program needs, from the catalogue sizes to bulk synthesis.

    • Candidate development
    • Patient-derived models
    • Preclinical candidate testing
    • Scale-up for preclinical work

By model system

From cell culture to in vivo studies

  • Compatible cell types

    Cell lines, primary cells, immune cells, stem cells and neurons, with the in vitro workflow.

  • 3D models, organoids and cancer cell types

    Spheroids, organoids and the cancer lines the compatibility page lists.

  • In vivo delivery

    The administration routes and sites, with no carrier required.